Treatment approach for IOPD. CRIM, cross-reactive immunologic... | Download Scientific Diagram
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect
Child Neurology: Pompe disease | Neurology
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine
Therapeutic Options for the Management of Pompe Disease: Current Chall | TCRM
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect
Kaplan-Meler survival analysis: overall and invasive ventilator-free... | Download Scientific Diagram
JCI Insight - Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine
IJNS | Free Full-Text | Newborn Screening for Pompe Disease: Pennsylvania Experience
Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
JCI Insight - Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
Targeted approaches to induce immune tolerance for Pompe disease therapy: Molecular Therapy Methods & Clinical Development
Efficacy of ERT+ITI in CRIM-negative IPD patients treated in the... | Download Table
JCI Insight - Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
Early ERT Key in Severe Classic Infantile Pompe, Study Finds
Algorithm for the Early Diagnosis and Treatment of Patients with Cross Reactive Immunologic Material- Negative Classic Infantile
Verification of CRIM status classification in patients with IOPD. | Download Table
Kaplan-Meier curve for overall survival of CRIM-negative IPD patients... | Download Scientific Diagram
CRIM status in PCMCs and fibroblasts, and GAA mutations, in 6 patients... | Download Table
The impact of antibodies on clinical outcomes in diseases treated with therapeutic protein: Lessons learned from infantile Pompe disease | Genetics in Medicine
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect
Pompe disease treatment: What are the options? | Pompe Disease News
